rare diseases

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Biotech

Analysts skeptical Applied can bring rare disease drug to market

Applied Therapeutics’ lack of progress on govorestat have led analysts to question whether the biotech will ever be able to get the drug to market.
James Waldron Nov 14, 2025 5:25am
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Lilly bags eye-catching gene therapy in $475M deal

Nov 10, 2025 7:00am
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FDA rejects Biohaven approval request, triggering cost cutting

Nov 5, 2025 4:02am
On target clinical trial success bullseye score

Sanofi's $1.7B bet beats CSL's Zemaira in phase 2 face-off

Oct 22, 2025 10:35am
purple lightning tornado

Electra shines with $183M fundraise for rare disease trial

Oct 22, 2025 8:26am
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Hansoh, Chugai ink separate and lucrative licensing agreements

Oct 17, 2025 11:04am